CRISPR Gene Therapy Cures Inherited Blood Disorder in Clinical Trial

Gene editing technology successfully eliminates sickle cell disease in trial participants.

CRISPR Gene Therapy Cures Inherited Blood Disorder in Clinical Trial
A landmark clinical trial has demonstrated that CRISPR gene editing can cure sickle cell disease, offering hope to millions worldwide. ## The Treatment Scientists used CRISPR to edit patients' own stem cells, correcting the genetic mutation that causes sickle cell disease. The modified cells were then reinfused into patients. ## Results All 45 trial participants have been effectively cured, with no serious adverse effects after three years of follow-up. Patients no longer experience the painful crises characteristic of the disease. ## Broader Implications This success proves that CRISPR can safely cure genetic diseases in humans, opening the door to treatments for thousands of other genetic conditions. ## Access Challenges The treatment currently costs over $2 million per patient. Researchers and policymakers are working to make it accessible to those who need it most.